Our Partners Working Together To Achieve Our Goals Our Partners Working Together ToAchieve Our Goals Combined BrainPatient WorthyChildren's Hospital of PhiladelphiaProbably GeneticRare Revolution MagazineAngel Flight NECoriell InstituteSimons SearchlightRARE-XPatient Airlift Services (PALS)Rare Epilepsy Network (REN)The Orphan Disease CenterCHAMP1 Research Foundation - EuropeGlobal Genes - Rare Foundation AllianceNational Organization for Rare Disorders (NORD)CHAMP1 UK